PODCAST

Status: S1LectNotes Time: 2025-03-11 Tags: lecturenotes Blood Links:

Content:

Objectives:

  • Outline the role os neutrophil elastase and alpha 1 antitrypsin in the acute phase response and in emphysema
  • Explain the molecular genetic basis of how variation in the SERPINA1 gene predispose to emphysema and liver disease
  • Outline a strategy to advise a patient who has a predisposing genotype the they should not smoke

Part 1

acute phase response

a 1 antitrypsin deficientcy (AAT) what is it one cause of Chronic obstructive pulmonary disease

background: acute inflammation response potential to damage normal tissues production of damaging proteins like elastase CRP can test well for inflammation

neutrophil elastase and emphysema elastase is in lysosome in neutrophils if accidentally released the damaging enzymes can damage lungs and liver AAT can stop this from happening it damages the liver as this is where AAT is produced and it can polymerize if not released

AAT is a protease inhibitor

SERine PROtease INhibitor diffuses into tissues so if there is elastase released it binds to the elastase is cleaved by jams the protease. 1:1 inhibitor (suicide inhibitor)

PART 2

common protease inhibitor genes PI * M is normal PI * Z common deficienct allele PI * S common in some populations PI * Null

ZZ leads to very high risk of COPD and Emphysema liver disease as well and neonatal hepatitis

SZ increases risk Znull high risk

MM no risk

normally inherited

codominant

determination can be made upon blood screen AAT inhibition activity IEF as well confounded by acute phase response

treatment is managing emphysema and COPD as well as iv AAT augmentation

maybe transplant

Smoking heavily affects ZZ individuals

convincing smokers to quit

Part 3